[Lysosome enzyme pseudodeficiency]

Rev Neurol (Paris). 2000 Nov;156(11):1005-12.
[Article in French]

Abstract

Inherited deficiency of lysosomal hydrolase often displays different clinical features. However, a greatly reduced enzyme activity may be observed in healthy individuals. This pseudo-deficiency concerns at least nine lysosomal hydrolases. When a deficiency has been proved, the presence of mutations known to cause pseudodeficiencies must be searched, above all in Tay-Sachs disease and metachromatic leukodystrophy.

Publication types

  • English Abstract
  • Review

MeSH terms

  • Cerebroside-Sulfatase / deficiency
  • Diagnosis, Differential
  • Gene Expression / genetics
  • Humans
  • Lysosomal Storage Diseases / diagnosis*
  • Lysosomal Storage Diseases / enzymology
  • Lysosomal Storage Diseases / genetics
  • Point Mutation / genetics
  • beta-N-Acetylhexosaminidases / deficiency

Substances

  • Cerebroside-Sulfatase
  • beta-N-Acetylhexosaminidases