Molecular studies and NK cell function of a new case of TAP2 homozygous human deficiency

Clin Exp Immunol. 2001 Aug;125(2):274-82. doi: 10.1046/j.1365-2249.2001.01595.x.

Abstract

In this paper we describe the clinical and molecular features of a new case (GOR) of homozygous human TAP2 deficiency, analysing the phenotype and function of NK cells. The patient presented from infancy with recurrent sinopulmonary infections; a selective IgG2 deficiency, negative antibody response to polysaccharide vaccination and low level of cell surface expression of HLA class I antigens were found. The sequence of TAP2 gene identified a single mutation, a C to T substitution changing the CGA arg codon at amino acid 220 into TGA stop codon in exon 3. By using MoAbs for KIRs, CD94, CD94/NKG2A and ILT2 we observed, in agreement with others, that the latter two receptors were overexpressed on TAP2-deficient NK cells. The inhibitory CD94/NKG2A and triggering CD94/NKG2C NK receptors, specific for HLA-E, appeared to be functional in a limited number of NK clones that could be expanded in vitro. Expression of HLA-E was virtually undetectable in GOR B-LCL and very faint in PBMC, further supporting that interactions of class I leader sequence nonamers with HLA-E in the ER depend on a functional TAP complex.

Publication types

  • Case Reports

MeSH terms

  • ATP Binding Cassette Transporter, Subfamily B, Member 2
  • ATP Binding Cassette Transporter, Subfamily B, Member 3
  • ATP-Binding Cassette Transporters / genetics*
  • ATP-Binding Cassette Transporters / metabolism
  • Amino Acid Sequence
  • Cells, Cultured
  • Cysteine Endopeptidases*
  • Cytotoxicity Tests, Immunologic
  • Histocompatibility Antigens Class I / metabolism
  • Homozygote
  • Humans
  • Immunophenotyping
  • K562 Cells
  • Killer Cells, Natural / immunology*
  • Molecular Sequence Data
  • Multienzyme Complexes*
  • Mutation
  • Proteasome Endopeptidase Complex
  • Proteins / metabolism
  • Severe Combined Immunodeficiency / genetics
  • Severe Combined Immunodeficiency / immunology*
  • T-Lymphocyte Subsets / classification

Substances

  • ATP Binding Cassette Transporter, Subfamily B, Member 2
  • ATP Binding Cassette Transporter, Subfamily B, Member 3
  • ATP-Binding Cassette Transporters
  • Histocompatibility Antigens Class I
  • Multienzyme Complexes
  • Proteins
  • TAP1 protein, human
  • LMP-2 protein
  • TAP2 protein, human
  • Cysteine Endopeptidases
  • LMP7 protein
  • Proteasome Endopeptidase Complex