Home treatment with enzyme replacement therapy in a 5-year-old girl with type 2 Gaucher disease

Pediatr Int. 2003 Jun;45(3):363-5. doi: 10.1046/j.1442-200x.2003.01725.x.
No abstract available

Publication types

  • Case Reports

MeSH terms

  • Child, Preschool
  • Female
  • Gaucher Disease / drug therapy*
  • Glucosylceramidase / therapeutic use*
  • Home Care Services, Hospital-Based*
  • Humans
  • Recombinant Proteins / therapeutic use*

Substances

  • Recombinant Proteins
  • Glucosylceramidase
  • imiglucerase