Variable phenotype in a P102L Gerstmann-Sträussler-Scheinker Italian family

Can J Neurol Sci. 2003 Aug;30(3):233-6. doi: 10.1017/s0317167100002651.

Abstract

Background: Gerstmann-Sträussler-Scheinker disease is an autosomal dominant prion disease. The clinical features include ataxia, dementia, spastic paraparesis and extrapyramidal signs.

Methods: We report a new large Italian family affected by Gerstmann-Sträussler-Scheinker disease.

Results: The four generation pedigree includes 11 patients. The mean age at onset +/- SD was 41.4 +/- 16.2 years. Mean disease duration to death in four patients was 5.5 +/- 1.7 years. Two clinical patterns were evident: cognitive impairment with scarce neurological features or ataxia followed by cognitive impairment. Molecular analysis showed P102L mutation in PRNP gene.

Conclusion: Three Italian families have been reported to date. The variable phenotype has already been reported, and does not appear related to the codon 129 polymorphism.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Aged
  • Amyloid / genetics*
  • Ataxia / etiology
  • Cerebellum / pathology
  • Cognition Disorders / etiology
  • Female
  • Gerstmann-Straussler-Scheinker Disease / complications
  • Gerstmann-Straussler-Scheinker Disease / diagnosis
  • Gerstmann-Straussler-Scheinker Disease / genetics*
  • Gerstmann-Straussler-Scheinker Disease / pathology
  • Humans
  • Italy
  • Magnetic Resonance Imaging
  • Male
  • Mutation*
  • Pedigree
  • Phenotype
  • Prion Proteins
  • Prions
  • Protein Precursors / genetics*

Substances

  • Amyloid
  • PRNP protein, human
  • Prion Proteins
  • Prions
  • Protein Precursors