Drug-loaded red blood cell-mediated clearance of HIV-1 macrophage reservoir by selective inhibition of STAT1 expression

J Leukoc Biol. 2003 Nov;74(5):764-71. doi: 10.1189/jlb.0403156. Epub 2003 Aug 21.

Abstract

Current highly active antiretroviral therapy (HAART) cannot eliminate HIV-1 from infected persons, mainly because of the existence of refractory viral reservoir(s). Beyond latently-infected CD4+-T lymphocytes, macrophages (M/M) are important persistent reservoirs for HIV in vivo, that represent a major obstacle to HIV-1 eradication. Therefore, a rational therapeutic approach directed to the selective elimination of long-living HIV-infected M/M may be relevant in the therapy of HIV infection. Here we report that HIV-1 chronic infection of human macrophages results in the marked increase of expression and phosphorylation of STAT1, a protein involved in the regulation of many functions such as cell growth, differentiation, and maintenance of cellular homeostasis, thereby providing a new molecular target for drug development. A single and brief exposure to 9-(beta-D-arabinofuranosyl)-2-fluoroadenine 5'-monophosphate (FaraAMP, Fludarabine), a potent antileukemic nucleoside analog active against STAT1 expressing cells, selectively kills macrophage cultures infected by HIV-1 without affecting uninfected macrophages. Furthermore, encapsulation of Fludarabine into autologous erythrocytes (RBC) and targeting to macrophages through a single-18 h treatment with drug-loaded RBC, not only abolishes the Fludarabine-mediated toxic effect on non-phagocytic cells, but also enhances the selective killing of HIV-infected macrophages. As a final result, a potent (>98%) and long-lasting (at least 4 weeks without rebound) inhibition of virus release from drug-loaded RBC-treated chronically-infected macrophages was achieved. Taken together, the evidence of HIV-1-induced increase of STAT1, and the availability of a selective drug targeting system, may prove useful in the design of new pharmacological treatments to clear the HIV-1 macrophage reservoir.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Acquired Immunodeficiency Syndrome / drug therapy
  • Acquired Immunodeficiency Syndrome / virology
  • Acute-Phase Proteins / antagonists & inhibitors
  • Antineoplastic Agents / pharmacology
  • Antiretroviral Therapy, Highly Active
  • Cell Survival / drug effects
  • Cells, Cultured
  • DNA-Binding Proteins / antagonists & inhibitors*
  • DNA-Binding Proteins / metabolism
  • Disease Reservoirs
  • Erythrocytes / physiology*
  • Erythrocytes / virology
  • HIV-1 / drug effects
  • HIV-1 / isolation & purification
  • HIV-1 / physiology*
  • Humans
  • Leukocytes, Mononuclear / cytology
  • Leukocytes, Mononuclear / virology
  • Macrophages / virology*
  • Proviruses / drug effects
  • STAT3 Transcription Factor
  • Trans-Activators / antagonists & inhibitors*
  • Trans-Activators / metabolism
  • Vidarabine / analogs & derivatives*
  • Vidarabine / blood
  • Vidarabine / pharmacology*
  • Viral Load
  • Virus Replication

Substances

  • Acute-Phase Proteins
  • Antineoplastic Agents
  • DNA-Binding Proteins
  • STAT3 Transcription Factor
  • STAT3 protein, human
  • Trans-Activators
  • Vidarabine
  • fludarabine