Chimerism and clinical outcomes of 110 recipients of unrelated donor bone marrow transplants who underwent conditioning with low-dose, single-exposure total body irradiation and cyclophosphamide

Blood. 2005 Apr 15;105(8):3035-41. doi: 10.1182/blood-2003-07-2346. Epub 2004 May 4.

Abstract

We hypothesized that low-dose (550-cGy), single-exposure, high dose rate (30 cGy/min) total body irradiation (TBI) with cyclophosphamide as conditioning for HLA-compatible unrelated donor (URD) bone marrow transplantation (BMT) would result in donor chimerism (DC) with a low risk for serious organ toxicity and treatment-related mortality (TRM). Twenty-six patients with good risk diagnoses (acute leukemia in first complete remission [CR] and chronic-phase chronic myelogenous leukemia [CML]) and 84 with poor risk diagnoses underwent this regimen and URD BMT. Unsorted marrow nucleated cells were assessed for chimerism using VNTR probes. All DC occurred in 78 (86%) of 91 evaluable patients at 1 or more follow-up points. Graft failure occurred in 7 (7.7%) patients. Fatal organ toxicity occurred in only 2% of patients. TRM rates through 2 years of follow-up were 19% and 42% in those with good and poor risk diagnoses, respectively. Overall and disease-free survival rates in the good risk group were 47% and 40%, respectively, and in the poor risk group they were 25% and 21%, respectively, at a median follow-up for living patients of 850 days (range, 354-1588 days). This regimen resulted in 100% DC in most patients undergoing URD BMT with a relatively low risk for fatal organ toxicity and TRM.

MeSH terms

  • Adult
  • Bone Marrow Transplantation* / adverse effects
  • Cyclophosphamide / administration & dosage*
  • Fever / etiology
  • Fever / mortality
  • Follow-Up Studies
  • Graft Survival
  • Graft vs Host Disease / etiology
  • Graft vs Host Disease / mortality
  • Histocompatibility Testing
  • Humans
  • Immunosuppressive Agents / administration & dosage*
  • Infections / etiology
  • Infections / mortality
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive / mortality
  • Leukemia, Myelogenous, Chronic, BCR-ABL Positive / therapy*
  • Middle Aged
  • Recovery of Function / immunology
  • Recurrence
  • Risk Factors
  • Transplantation Chimera*
  • Transplantation Conditioning / methods
  • Treatment Outcome
  • Whole-Body Irradiation*

Substances

  • Immunosuppressive Agents
  • Cyclophosphamide