Lentiviral shRNA silencing of murine bone marrow cell CCR2 leads to persistent knockdown of CCR2 function in vivo

Blood. 2005 Aug 15;106(4):1147-53. doi: 10.1182/blood-2004-12-4839. Epub 2005 May 10.

Abstract

A major barrier in hematopoietic gene function studies is posed by the laborious and time-consuming generation of knockout mice with an appropriate genetic background. Here we present a novel lentivirus-based strategy for the in situ generation of hematopoietic knockdowns. A short hairpin RNA (shRNA) was designed targeting murine CC-chemokine receptor 2 (CCR2), which was able to specifically blunt CCR2 expression at the mRNA, protein, and functional levels in vitro. Reconstitution of irradiated recipient mice with autologous bone marrow that had been ex vivo transduced with shRNA lentivirus led to persistent down-regulation of CCR2 expression, which translated into a 70% reduction in CCR2-dependent recruitment of macrophages to an inflamed peritoneal cavity without noticeable side effects on related chemokine receptors or general inflammation status. These findings clearly demonstrate the potential of shRNA lentivirus-infected bone marrow transplantation as a rapid and effective method to generate hematopoietic knockdowns for leukocyte gene function studies.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Bone Marrow Cells
  • Bone Marrow Transplantation
  • Chemotaxis
  • Down-Regulation
  • Lentivirus / genetics*
  • Macrophages
  • Methods
  • Mice
  • Mice, Inbred C57BL
  • Mice, Knockout
  • Models, Animal*
  • RNA Interference
  • RNA, Messenger / drug effects
  • RNA, Small Interfering / chemical synthesis
  • RNA, Small Interfering / genetics*
  • RNA, Small Interfering / pharmacology
  • Receptors, CCR2
  • Receptors, Chemokine / deficiency*
  • Receptors, Chemokine / drug effects
  • Receptors, Chemokine / genetics
  • Transduction, Genetic

Substances

  • Ccr2 protein, mouse
  • RNA, Messenger
  • RNA, Small Interfering
  • Receptors, CCR2
  • Receptors, Chemokine