Hermansky-Pudlak syndrome with a novel mutation

Intern Med. 2005 Jul;44(7):733-8. doi: 10.2169/internalmedicine.44.733.

Abstract

We report a case of Hermansky-Pudlak syndrome (HPS) with a novel mutation in the HPS1 gene. This case showed oculocutaneous albinism and lysosomal ceroid accumulation, however platelet dysfunction was not observed. Histopathological findings of the biopsied lung tissue were compatible with HPS. Sequencing analysis showed the insertion of C in the codon 178 (739 bp) of the HPS1 gene forming a stop codon at codon 181. To the best of our knowledge, this is a novel HPS1 gene mutation.

Publication types

  • Case Reports

MeSH terms

  • Comorbidity
  • Female
  • Frameshift Mutation / genetics*
  • Hermanski-Pudlak Syndrome / epidemiology
  • Hermanski-Pudlak Syndrome / genetics*
  • Hermanski-Pudlak Syndrome / pathology
  • Humans
  • Lung / pathology
  • Lung Diseases, Interstitial / epidemiology
  • Membrane Proteins / genetics*
  • Middle Aged
  • Sequence Analysis, DNA

Substances

  • HPS1 protein, human
  • Membrane Proteins