Green tea (-)-epigallocatechin-gallate modulates early events in huntingtin misfolding and reduces toxicity in Huntington's disease models

Hum Mol Genet. 2006 Sep 15;15(18):2743-51. doi: 10.1093/hmg/ddl210. Epub 2006 Aug 7.

Abstract

Huntington's disease (HD) is a progressive neurodegenerative disorder for which only symptomatic treatments of limited effectiveness are available. Preventing early misfolding steps and thereby aggregation of the polyglutamine (polyQ)-containing protein huntingtin (htt) in neurons of patients may represent an attractive therapeutic strategy to postpone the onset and progression of HD. Here, we demonstrate that the green tea polyphenol (-)-epigallocatechin-3-gallate (EGCG) potently inhibits the aggregation of mutant htt exon 1 protein in a dose-dependent manner. Dot-blot assays and atomic force microscopy studies revealed that EGCG modulates misfolding and oligomerization of mutant htt exon 1 protein in vitro, indicating that it interferes with very early events in the aggregation process. Also, EGCG significantly reduced polyQ-mediated htt protein aggregation and cytotoxicity in an yeast model of HD. When EGCG was fed to transgenic HD flies overexpressing a pathogenic htt exon 1 protein, photoreceptor degeneration and motor function improved. These results indicate that modulators of htt exon 1 misfolding and oligomerization like EGCG are likely to reduce polyQ-mediated toxicity in vivo. Our studies may provide the basis for the development of a novel pharmacotherapy for HD and related polyQ disorders.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Animals, Genetically Modified
  • Camellia sinensis / chemistry
  • Catechin / analogs & derivatives*
  • Catechin / pharmacology
  • Drosophila melanogaster / genetics
  • Exons
  • Humans
  • Huntingtin Protein
  • Huntington Disease / drug therapy*
  • Huntington Disease / genetics
  • Huntington Disease / metabolism
  • In Vitro Techniques
  • Microscopy, Atomic Force
  • Models, Biological
  • Motor Neurons / drug effects
  • Multiprotein Complexes
  • Mutation
  • Nerve Degeneration / drug therapy
  • Nerve Tissue Proteins / chemistry*
  • Nerve Tissue Proteins / drug effects*
  • Nerve Tissue Proteins / genetics
  • Nuclear Proteins / chemistry*
  • Nuclear Proteins / drug effects*
  • Nuclear Proteins / genetics
  • Photoreceptor Cells, Invertebrate / drug effects
  • Phytotherapy
  • Protein Conformation / drug effects
  • Protein Folding
  • Protein Structure, Quaternary / drug effects
  • Recombinant Fusion Proteins / chemistry
  • Recombinant Fusion Proteins / drug effects
  • Recombinant Fusion Proteins / genetics
  • Saccharomyces cerevisiae / chemistry
  • Saccharomyces cerevisiae / drug effects
  • Saccharomyces cerevisiae / genetics

Substances

  • HTT protein, human
  • Huntingtin Protein
  • Multiprotein Complexes
  • Nerve Tissue Proteins
  • Nuclear Proteins
  • Recombinant Fusion Proteins
  • Catechin
  • epigallocatechin gallate