Induction of chimerism in rhesus macaques through stem cell transplant and costimulation blockade-based immunosuppression

Am J Transplant. 2007 Feb;7(2):320-35. doi: 10.1111/j.1600-6143.2006.01622.x.

Abstract

A strategy for producing high-level hematopoietic chimerism after non-myeloablative conditioning has been established in the rhesus macaque. This strategy relies on hematopoietic stem cell transplantation after induction with a non-myeloablative dose of busulfan and blockade of the IL2-receptor in the setting of mTOR inhibition with sirolimus and combined CD28/CD154 costimulation blockade. Hematopoietic stem cells derived from bone marrow and leukopheresis products both were found to be successful in inducing high-level chimerism. Mean peripheral blood peak donor chimerism was 81% with a median chimerism duration of 145 days. Additional immune modulation strategies, such as pre-transplant CD8 depletion, donor-specific transfusion, recipient thymectomy or peritransplant deoxyspergualin treatment did not improve the level or durability of chimerism. Recipient immunologic assessment suggested that chimerism occurred amidst donor-specific down-regulation of alloreactive T cells, and the reappearance of vigorous T-mediated alloreactivity accompanied rejection of the transplants. Furthermore, viral reactivation constituted a significant transplant-related toxicity and may have negatively impacted the ability to achieve indefinite survival of transplanted stem cells. Nevertheless, this chimerism-induction regimen induced amongst the longest-lived stem cell chimerism reported to date for non-human primates and thus represents a platform upon which to evaluate emerging tolerance-induction strategies.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Bone Marrow Transplantation / methods
  • Busulfan / pharmacology
  • Chimerism*
  • Cytomegalovirus Infections / complications
  • Hematopoietic Stem Cell Transplantation / methods*
  • Immunosuppression Therapy / methods*
  • Immunosuppressive Agents / pharmacology
  • Leukapheresis / methods
  • Macaca mulatta / genetics
  • Macaca mulatta / immunology*
  • Receptors, Interleukin-2 / antagonists & inhibitors
  • Sirolimus / pharmacology
  • T-Lymphocytes / immunology
  • Transplantation Tolerance

Substances

  • Immunosuppressive Agents
  • Receptors, Interleukin-2
  • Busulfan
  • Sirolimus