Semliki Forest virus vectors expressing transforming growth factor beta inhibit experimental autoimmune encephalomyelitis in Balb/c mice

Biochem Biophys Res Commun. 2007 Apr 13;355(3):776-81. doi: 10.1016/j.bbrc.2007.02.026. Epub 2007 Feb 14.

Abstract

Cytokine immunomodulation of experimental autoimmune encephalomyelitis (EAE), a model for multiple sclerosis, has remained a formidable treatment option, but access into the CNS is hampered due to the impermeability of the blood-brain barrier. In this report, we describe the construction and characterization of CNS-homing gene delivery/therapy vectors based on avirulent Semliki Forest virus (SFV) expressing either native or mutant transforming growth factor beta 1 (TGF-beta1). Biological activity of the expressed inserts was demonstrated by PAI-1 promoter driven luciferase production in mink cells and TGF-beta1 mRNA was demonstrated in the CNS of virus treated mice by in situ hybridization and RT-PCR. Both vectors, when given intraperitoneally to EAE mice significantly reduced disease severity compared to untreated mice. Our results imply that immunomodulation by neurotropic viral vectors may offer a promising treatment strategy for autoimmune CNS disorders.

Publication types

  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Brain / metabolism
  • Brain Chemistry
  • Encephalomyelitis, Autoimmune, Experimental / therapy*
  • Female
  • Genetic Therapy*
  • Genetic Vectors / genetics*
  • Immunotherapy*
  • Mice
  • Mice, Inbred BALB C
  • Protein Biosynthesis
  • RNA, Messenger / analysis
  • RNA, Messenger / metabolism
  • Semliki forest virus / genetics*
  • Transforming Growth Factor beta1 / genetics*
  • Transforming Growth Factor beta1 / metabolism

Substances

  • RNA, Messenger
  • Transforming Growth Factor beta1