A severely affected female infant with x-linked dominant chondrodysplasia punctata: a case report and a brief review of the literature

Pediatr Dev Pathol. 2007 Mar-Apr;10(2):142-8. doi: 10.2350/06-06-0111.1.

Abstract

We recently performed an autopsy on a premature female newborn with rhizomesoacromelic limb shortening of the upper and lower extremities, craniofacial dysmorphism, and chondrodysplasia punctata. A diagnosis of Conradi-Hunermann-Happle syndrome or X-linked dominant chondrodysplasia punctata was made based on elevated cholest-8(9)-ene-3beta-ol in serum and tissues. Molecular analysis of EBP, mutations of which are responsible for this malformation syndrome, revealed a monoallelic missense mutation, c.328 G>A (R110Q). We present this case as an illustration of an unusually severe manifestation of this disorder in a female, with additional unusual features including lack of skin manifestations and apparent bilateral symmetry of the skeletal findings.

Publication types

  • Case Reports
  • Review

MeSH terms

  • Chondrodysplasia Punctata / diagnosis*
  • Chondrodysplasia Punctata / diagnostic imaging
  • Chondrodysplasia Punctata / genetics*
  • Chondrodysplasia Punctata / pathology
  • Fatal Outcome
  • Female
  • Genes, Dominant*
  • Genes, X-Linked*
  • Humans
  • Infant, Newborn
  • Infant, Premature
  • Models, Biological
  • Mutation, Missense
  • Pregnancy
  • Radiography
  • Severity of Illness Index
  • Steroid Isomerases / blood
  • Steroid Isomerases / genetics*
  • Steroid Isomerases / metabolism

Substances

  • Steroid Isomerases
  • EBP protein, human