The suicide gene therapy challenge: how to improve a successful gene therapy approach

Mol Ther. 2007 Jul;15(7):1248-52. doi: 10.1038/sj.mt.6300190. Epub 2007 May 8.

Abstract

The transfer of a suicide gene into donor lymphocytes to control alloreactivity in the context of allogeneic hematopoietic stem cell transplantation (allo-HSCT) represents the widest clinical application of T-cell based gene transfer, as shown by more than 100 patients treated worldwide to date, several phase I-II studies completed, and a registrative phase III study, sponsored by a biotech firm, about to begin. In this mini-review, we will summarize the clinical results obtained to date, and attempt to identify the steps envisaged to optimize the suicide gene therapy approach.

Publication types

  • Review

MeSH terms

  • Animals
  • Genes, Transgenic, Suicide / genetics*
  • Genetic Therapy / methods*
  • Hematopoietic Stem Cell Transplantation
  • Humans
  • Prodrugs / pharmacology
  • T-Lymphocytes / drug effects
  • T-Lymphocytes / immunology
  • T-Lymphocytes / metabolism
  • Treatment Outcome

Substances

  • Prodrugs