Novel insight into the agonistic mechanism of alefacept in vivo: differentially expressed genes may serve as biomarkers of response in psoriasis patients

J Immunol. 2007 Jun 1;178(11):7442-9. doi: 10.4049/jimmunol.178.11.7442.

Abstract

Alefacept is an LFA3-Ig fusion protein that binds to CD2 and is thought to inhibit T cell activation by antagonism of CD2 signaling or by lysis of CD2(+) cells. Alefacept is potential future therapeutic for organ transplant recipients or graft-vs-host disease and is an approved therapeutic for psoriasis vulgaris, which is a T cell-mediated inflammatory disease. However, alefacept improves psoriasis in only approximately 50% of patients treated for 12 wk. We studied the immunologic effects of alefacept in a group of psoriasis patients during treatment. We found that T cells, especially CD8(+) T cells, were rapidly decreased in the peripheral circulation. Decreases in circulating T cells were not associated with induced apoptosis. Unexpectedly, in addition to suppression of inflammatory genes, we found a marked induction of mRNAs for STAT1, IL-8, and monokine induced by IFN-gamma during the first day of treatment in PBMC. We confirmed the agonistic effects of alefacept in PBMC in vitro, which were similar to CD3/CD28 ligation on T cells. These data establish that alefacept activates gene expression programs in leukocytes and suggest that its therapeutic action may be as a mixed agonist/antagonist. Furthermore, responding patients to alefacept treatment show unique patterns of gene modulation. Whereas alefacept down-regulated TCRs CD3D and CD2 in responders, nonresponders reveal a higher expression of T cell activation genes such as CD69 in pretreatment PBMC. These finding suggest a potential basis for categorizing responders vs nonresponders at an early time point in treatment or before treatment of a broad range of proinflammatory diseases. This study 1) establishes alefacept as a novel CD2 agonist molecule for induction of leukocyte activation genes (prior work proposed its mechanism as a CD2 antagonist) and 2) that differential activation of genes may categorize clinical responders to this agent, critical for cost-effective use of this drug.

Publication types

  • Comparative Study
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Validation Study

MeSH terms

  • Adult
  • Aged
  • Alefacept
  • Apoptosis / genetics
  • Apoptosis / immunology
  • Biomarkers / blood
  • CD2 Antigens / biosynthesis
  • CD2 Antigens / genetics
  • CD8-Positive T-Lymphocytes / immunology
  • CD8-Positive T-Lymphocytes / metabolism
  • CD8-Positive T-Lymphocytes / pathology
  • Down-Regulation / genetics
  • Down-Regulation / immunology
  • Female
  • Gene Expression Regulation / immunology*
  • Humans
  • Immunologic Memory / genetics
  • Lymphocyte Activation / genetics
  • Lymphopenia / genetics
  • Lymphopenia / immunology
  • Lymphopenia / pathology
  • Male
  • Middle Aged
  • Protein Binding / genetics
  • Protein Binding / immunology
  • Psoriasis / genetics
  • Psoriasis / immunology*
  • Psoriasis / pathology
  • Psoriasis / therapy*
  • Recombinant Fusion Proteins / administration & dosage*
  • Recombinant Fusion Proteins / agonists*
  • Recombinant Fusion Proteins / metabolism
  • Recombinant Fusion Proteins / therapeutic use
  • Resting Phase, Cell Cycle / genetics
  • Resting Phase, Cell Cycle / immunology
  • Skin / immunology
  • Skin / metabolism
  • Skin / pathology
  • T-Lymphocyte Subsets / immunology
  • T-Lymphocyte Subsets / metabolism
  • T-Lymphocyte Subsets / pathology
  • Up-Regulation / genetics
  • Up-Regulation / immunology

Substances

  • Biomarkers
  • CD2 Antigens
  • Recombinant Fusion Proteins
  • Alefacept