Membrane-active peptides for non-viral gene therapy: making the safest easier

Trends Biotechnol. 2008 May;26(5):267-75. doi: 10.1016/j.tibtech.2008.02.003. Epub 2008 Mar 20.

Abstract

Non-viral gene therapy uses engineered nanoparticles in the virus size range for the cell-targeted delivery of therapeutic nucleic acids. A diverse range of macromolecules are suitable for constructing such 'artificial viruses'. However, proteins, either man-made or from natural sources, are especially convenient for mimicking the viral functions critical for gene transfer. Cell penetration is a critical step for the delivery of nucleic acids in sufficient amounts and hence for reaching satisfactory transgene expression levels. Membrane-active peptides have shown great promise because of their positive role in cross-membrane transport and intracellular trafficking, and they have been incorporated into different artificial viruses. In this review, we will discuss the biological properties of these peptides together with the newest rational approaches designed to optimize their application.

Publication types

  • Research Support, Non-U.S. Gov't
  • Review

MeSH terms

  • Animals
  • Biological Transport / drug effects
  • DNA / chemistry
  • DNA / genetics
  • DNA / metabolism
  • Gene Transfer Techniques*
  • Genetic Therapy / methods*
  • Humans
  • Intracellular Membranes / metabolism
  • Models, Biological
  • Peptides / chemistry
  • Peptides / pharmacology

Substances

  • Peptides
  • DNA