Pharmacological interventions for nonalcoholic fatty liver disease in adults and in children: a systematic review

J Pediatr Gastroenterol Nutr. 2009 May;48(5):587-96. doi: 10.1097/MPG.0b013e31818e04d1.

Abstract

Background: Uncertainty exists regarding the treatment of patients with nonalcoholic fatty liver disease (NAFLD) who are unable to lose weight and/or change lifestyle. The present study assesses the effectiveness and safety of pharmacological and dietary supplement interventions for NAFLD.

Methods: MEDLINE, EMBASE, and the Cochrane Library were searched for randomized controlled trials (RCTs) both in adults and in children.

Results: Fifteen (2 pediatric patients and 13 adults) RCTs met the inclusion criteria. A significant effect on normalization of alanine transaminase was found in patients treated with metformin compared with vitamin E, and in those treated with high-dose (3 g) carnitine vs diet. In contrast, there was no difference in patients treated with pioglitazone combined with vitamin E versus vitamin E alone, ursodeoxycholic acid (UDCA) combined with vitamin E or alone versus placebo, or UDCA versus combination of vitamin E and vitamin C, and in patients treated with vitamin E, probucol, N-acetylcysteine, low doses of carnitine, or Yo Jyo Shi Ko compared with placebo. Aspartate aminotransferase normalization was significantly higher in those treated with UDCA combined with vitamin E versus UDCA alone or placebo, and in those treated with metformin. Small number of subjects, high drop-out rates, and numerous interventions in 1 study limit the value of many studies. Only 7 RCTs analyzed biopsy specimens, but most of them have significant methodological limitations. Pioglitazone had reduced liver necrosis and inflammation in 1 large study.

Conclusions: Limited data do not allow one to draw firm conclusions on the efficacy of various treatments for NAFLD.

Publication types

  • Review
  • Systematic Review

MeSH terms

  • Acetylcysteine / therapeutic use
  • Adult
  • Alanine Transaminase / analysis
  • Aspartate Aminotransferases / analysis*
  • Carnitine / therapeutic use
  • Child
  • Dietary Supplements*
  • Drug Synergism
  • Drug Therapy, Combination
  • Fatty Liver / diet therapy
  • Fatty Liver / drug therapy*
  • Fatty Liver / pathology
  • Humans
  • Hypoglycemic Agents / therapeutic use*
  • Liver / pathology
  • Metformin / therapeutic use*
  • Pioglitazone
  • Probucol / therapeutic use
  • Randomized Controlled Trials as Topic
  • Thiazolidinediones / therapeutic use
  • Ursodeoxycholic Acid / therapeutic use
  • Vitamin E / therapeutic use

Substances

  • Hypoglycemic Agents
  • Thiazolidinediones
  • Vitamin E
  • Ursodeoxycholic Acid
  • Metformin
  • Aspartate Aminotransferases
  • Alanine Transaminase
  • Probucol
  • Carnitine
  • Acetylcysteine
  • Pioglitazone