Axial spondylometaphyseal dysplasia: Confirmation and further delineation of a new SMD with retinal dystrophy

Am J Med Genet A. 2010 Jun;152A(6):1550-4. doi: 10.1002/ajmg.a.33397.

Abstract

This report describes two unrelated boys presenting with short stature, femoral metaphyseal abnormalities, platyspondyly, and retinitis pigmentosa. Patients share similar findings with cases described by Ehara et al. [Ehara et al. (1997); Eur J Pediatr 156:627-630] described as axial spondylometaphyseal dysplasia. The presence of consanguinity in one of our patients further supports an autosomal recessive mode of inheritance of what, we believe, constitutes a separate and distinct entity.

Publication types

  • Case Reports

MeSH terms

  • Adolescent
  • Child
  • Femur / abnormalities*
  • Growth Disorders / diagnosis*
  • Growth Disorders / genetics
  • Humans
  • Male
  • Osteochondrodysplasias / diagnosis*
  • Osteochondrodysplasias / diagnostic imaging
  • Osteochondrodysplasias / genetics
  • Radiography
  • Retinal Degeneration / diagnosis*
  • Retinal Degeneration / genetics
  • Retinitis Pigmentosa / diagnosis*
  • Retinitis Pigmentosa / genetics
  • Syndrome