Accumulation of toxic α-synuclein oligomer within endoplasmic reticulum occurs in α-synucleinopathy in vivo

J Neurosci. 2012 Mar 7;32(10):3301-5. doi: 10.1523/JNEUROSCI.5368-11.2012.

Abstract

In Parkinson's disease (PD) and other α-synucleinopathies, prefibrillar α-synuclein (αS) oligomer is implicated in the pathogenesis. However, toxic αS oligomers observed using in vitro systems are not generally seen to be associated with α-synucleinopathy in vivo. Thus, the pathologic significance of αS oligomers to αS neurotoxicity is unknown. Herein, we show that, αS that accumulate within endoplasmic reticulum (ER)/microsome forms toxic oligomers in mouse and human brain with the α-synucleinopathy. In the mouse model of α-synucleinopathy, αS oligomers initially form before the onset of disease and continue to accumulate with the disease progression. Significantly, treatment of αS transgenic mice with Salubrinal, an anti-ER stress compound that delays the onset of disease, reduces ER accumulation of αS oligomers. These results indicate that αS oligomers with toxic conformation accumulate in ER, and αS oligomer-dependent ER stress is pathologically relevant for PD.

Publication types

  • Comparative Study
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Animals
  • Disease Models, Animal
  • Disease Progression
  • Endoplasmic Reticulum / metabolism*
  • Endoplasmic Reticulum / pathology*
  • Humans
  • Mice
  • Mice, Transgenic
  • Nucleic Acid Conformation
  • Oligonucleotides / metabolism*
  • Oligonucleotides / toxicity*
  • Oxidative Stress / genetics
  • Parkinson Disease / genetics
  • Parkinson Disease / metabolism
  • Parkinson Disease / pathology
  • alpha-Synuclein / metabolism*
  • alpha-Synuclein / toxicity*

Substances

  • Oligonucleotides
  • alpha-Synuclein