Tadalafil crosses the blood-brain barrier and reverses cognitive dysfunction in a mouse model of AD

Neuropharmacology. 2013 Jan:64:114-23. doi: 10.1016/j.neuropharm.2012.06.052. Epub 2012 Jul 7.

Abstract

Previous studies have demonstrated that cognitive function can be restored in mouse models of Alzheimer's disease (AD) following administration of sildenafil, a specific PDE5 inhibitor (Puzzo et al., 2009; Cuadrado-Tejedor et al.). Another very potent PDE5 inhibitor with a longer half-life and safe in chronic treatments, tadalafil, may represent a better alternative candidate for AD therapy. However, tadalafil was proven unable to achieve similar benefits than those of sildenafil in AD animal models (Puzzo et al., 2009). The lack of efficacy was attributed to inability to cross the blood-brain barrier (BBB). In this paper we first measured the blood and brain levels of tadalafil to prove that the compound crosses BBB and that chronic treatment leads to accumulation in the brain of the J20 transgenic mouse model of AD. We demonstrated the presence of PDE5 mRNA in the brain of the mice and also in the human brain. After a 10 week treatment with either of these PDE5 inhibitors, the performance of the J20 mice in the Morris water maze test improved when compared with the transgenic mice that received vehicle. Biochemical analysis revealed that neither sildenafil nor tadalafil altered the amyloid burden, although both compounds reduced Tau phosphorylation in the mouse hippocampus. This study provides evidence of the potential benefits of a chronic tadalafil treatment in AD therapy. This article is part of a Special Issue entitled 'Cognitive Enhancers'.

Publication types

  • Comparative Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Alzheimer Disease / drug therapy*
  • Alzheimer Disease / genetics
  • Alzheimer Disease / metabolism
  • Animals
  • Blood-Brain Barrier / metabolism*
  • Brain / drug effects
  • Brain / metabolism
  • Brain / pathology
  • Carbolines / blood
  • Carbolines / metabolism
  • Carbolines / pharmacokinetics*
  • Carbolines / therapeutic use
  • Cognition Disorders / etiology
  • Cognition Disorders / prevention & control*
  • Cyclic Nucleotide Phosphodiesterases, Type 5 / genetics
  • Cyclic Nucleotide Phosphodiesterases, Type 5 / metabolism
  • Disease Models, Animal*
  • Female
  • Gene Expression Regulation, Enzymologic / drug effects
  • Half-Life
  • Humans
  • Macaca fascicularis
  • Male
  • Mice
  • Mice, Inbred C57BL
  • Mice, Transgenic
  • Nootropic Agents / blood
  • Nootropic Agents / metabolism
  • Nootropic Agents / pharmacokinetics*
  • Nootropic Agents / therapeutic use
  • Phosphodiesterase 5 Inhibitors / blood
  • Phosphodiesterase 5 Inhibitors / metabolism
  • Phosphodiesterase 5 Inhibitors / pharmacokinetics*
  • Phosphodiesterase 5 Inhibitors / therapeutic use
  • Piperazines / therapeutic use
  • Purines / therapeutic use
  • Sildenafil Citrate
  • Species Specificity
  • Sulfones / therapeutic use
  • Tadalafil
  • Tissue Distribution

Substances

  • Carbolines
  • Nootropic Agents
  • Phosphodiesterase 5 Inhibitors
  • Piperazines
  • Purines
  • Sulfones
  • Tadalafil
  • Sildenafil Citrate
  • Cyclic Nucleotide Phosphodiesterases, Type 5