Transient cytokine treatment induces acinar cell reprogramming and regenerates functional beta cell mass in diabetic mice

Nat Biotechnol. 2014 Jan;32(1):76-83. doi: 10.1038/nbt.2747. Epub 2013 Nov 17.

Abstract

Reprogramming of pancreatic exocrine cells into cells resembling beta cells may provide a strategy for treating diabetes. Here we show that transient administration of epidermal growth factor and ciliary neurotrophic factor to adult mice with chronic hyperglycemia efficiently stimulates the conversion of terminally differentiated acinar cells to beta-like cells. Newly generated beta-like cells are epigenetically reprogrammed, functional and glucose responsive, and they reinstate normal glycemic control for up to 248 d. The regenerative process depends on Stat3 signaling and requires a threshold number of Neurogenin 3 (Ngn3)-expressing acinar cells. In contrast to previous work demonstrating in vivo conversion of acinar cells to beta-like cells by viral delivery of exogenous transcription factors, our approach achieves acinar-to-beta-cell reprogramming through transient cytokine exposure rather than genetic modification.

Publication types

  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't
  • Retracted Publication

MeSH terms

  • Acinar Cells / drug effects
  • Acinar Cells / pathology
  • Animals
  • Cell Differentiation / drug effects
  • Cell Proliferation / drug effects
  • Ciliary Neurotrophic Factor / administration & dosage*
  • Ciliary Neurotrophic Factor / genetics
  • Diabetes Mellitus / drug therapy*
  • Diabetes Mellitus / genetics
  • Epidermal Growth Factor / administration & dosage*
  • Epidermal Growth Factor / genetics
  • Hyperglycemia / drug therapy
  • Insulin-Secreting Cells / drug effects*
  • Insulin-Secreting Cells / pathology
  • Mice
  • Mice, Inbred NOD / genetics
  • Signal Transduction

Substances

  • Ciliary Neurotrophic Factor
  • Epidermal Growth Factor