Opportunities and challenges in developing stearoyl-coenzyme A desaturase-1 inhibitors as novel therapeutics for human disease

J Med Chem. 2014 Jun 26;57(12):5039-56. doi: 10.1021/jm401516c. Epub 2013 Dec 20.

Abstract

This review provides an overview of stearoyl-coenzyme A desaturase-1 (SCD1) as a novel therapeutic target for metabolic disorders and other indications. Target validation is reviewed, and limitations due to incomplete knowledge of the relevant biological systems are described. Assay development, particularly for high throughput screening, and characterization of SCD1 inhibition are summarized. The progress and evolution in medicinal chemistry are discussed, specifically focusing on key attributes of the most advanced SCD1 inhibitors described in the primary literature and in patent applications. This work culminated in numerous companies identifying potent selective inhibitors, some of which progressed to early clinical development. The status of current SCD1 drug discovery programs is reviewed. Challenges are discussed, and potential new directions are indicated.

Publication types

  • Review

MeSH terms

  • Animals
  • Humans
  • Lipid Metabolism
  • Metabolic Diseases / drug therapy*
  • Metabolic Diseases / enzymology
  • Molecular Targeted Therapy
  • Stearoyl-CoA Desaturase / antagonists & inhibitors*
  • Stearoyl-CoA Desaturase / genetics
  • Stearoyl-CoA Desaturase / metabolism

Substances

  • SCD1 protein, human
  • Stearoyl-CoA Desaturase