Beyond small-molecule SAR: using the dopamine D3 receptor crystal structure to guide drug design

Adv Pharmacol. 2014:69:267-300. doi: 10.1016/B978-0-12-420118-7.00007-X.

Abstract

The dopamine D3 receptor is a target of pharmacotherapeutic interest in a variety of neurological disorders including schizophrenia, restless leg syndrome, and drug addiction. The high protein sequence homology between the D3 and D2 receptors has posed a challenge to developing D3 receptor-selective ligands whose behavioral actions can be attributed to D3 receptor engagement, in vivo. However, through primarily small-molecule structure-activity relationship (SAR) studies, a variety of chemical scaffolds have been discovered over the past two decades that have resulted in several D3 receptor-selective ligands with high affinity and in vivo activity. Nevertheless, viable clinical candidates remain limited. The recent determination of the high-resolution crystal structure of the D3 receptor has invigorated structure-based drug design, providing refinements to the molecular dynamic models and testable predictions about receptor-ligand interactions. This chapter will highlight recent preclinical and clinical studies demonstrating potential utility of D3 receptor-selective ligands in the treatment of addiction. In addition, new structure-based rational drug design strategies for D3 receptor-selective ligands that complement traditional small-molecule SAR to improve the selectivity and directed efficacy profiles are examined.

Keywords: Addiction; Crystal structure; Pharmacology; Receptor homology modeling; Structure–activity relationships.

Publication types

  • Research Support, N.I.H., Extramural
  • Review

MeSH terms

  • Animals
  • Binding Sites / physiology
  • Crystallography, X-Ray
  • Dopamine Agents / chemistry
  • Dopamine Agents / metabolism
  • Dopamine Agents / therapeutic use
  • Drug Design*
  • Humans
  • Protein Binding / physiology
  • Receptors, Dopamine D3 / chemistry*
  • Receptors, Dopamine D3 / metabolism*
  • Receptors, Dopamine D3 / physiology
  • Structure-Activity Relationship
  • Substance-Related Disorders / drug therapy
  • Substance-Related Disorders / metabolism

Substances

  • Dopamine Agents
  • Receptors, Dopamine D3