Letter to the Editors: Concerning "Long-term safety and efficacy of AAV gene therapy in the canine model of glycogen storage disease type Ia" by Lee et al
J Inherit Metab Dis
.
2018 Nov;41(6):913-914.
doi: 10.1007/s10545-018-0248-2.
Epub 2018 Sep 25.
Authors
Elizabeth D Brooks
1
2
,
Priya S Kishnani
1
,
Dwight D Koeberl
3
Affiliations
1
Division of Medical Genetics, Duke University Medical Center, DUMC Box 103856, Durham, NC, 27710, USA.
2
Division of Laboratory Animal Resources, Duke University Medical Center, Durham, NC, USA.
3
Division of Medical Genetics, Duke University Medical Center, DUMC Box 103856, Durham, NC, 27710, USA. dwight.koeberl@duke.edu.
PMID:
30255460
PMCID:
PMC6501822
DOI:
10.1007/s10545-018-0248-2
No abstract available
Publication types
Letter
Comment
MeSH terms
Animals
Dogs
Genetic Therapy
Glycogen Storage Disease Type I*
Supplementary concepts
Hepatorenal form of glycogen storage disease
Grants and funding
R01 DK105434/DK/NIDDK NIH HHS/United States