Single-Dose Pharmacokinetics, Safety, and Tolerability of Avadomide (CC-122) in Subjects With Mild, Moderate, or Severe Renal Impairment

Clin Pharmacol Drug Dev. 2020 Oct;9(7):785-796. doi: 10.1002/cpdd.760. Epub 2019 Dec 31.

Abstract

CC-122 (Avadomide) is a nonphthalimide analogue of thalidomide that has multiple pharmacological activities including immune modulation of several immune cell subsets, antigrowth activity, antiproliferative activity, and antiangiogenic activity. CC-122 as monotherapy and in combination with other agents is being evaluated for multiple indications including hematologic malignancies and advanced solid tumors. Given that renal clearance is one of the major routes of elimination for CC-122 and its clearance/exposure could be affected by renal impairment, a total of 50 subjects with various degrees of renal function were enrolled in an open-label, single-dose study to evaluate the impact of renal impairment on CC-122 pharmacokinetic disposition. The study showed that following administration of a single oral dose of 3 mg CC-122, renal impairment reduced both the apparent total plasma clearance and renal clearance of CC-122, but it had less impact on CC-122 absorption, as demonstrated by similar Tmax and Cmax among groups with various degrees of renal function. Compared with exposure in subjects with normal renal function, total plasma exposure to CC-122 increased by ∼20%, ∼50%, and ∼120% in subjects with mild, moderate, and severe renal insufficiency, respectively. Results from this study combined with modeling/simulation suggest that dose adjustments are necessary in patients with moderate or severe but not with mild renal impairment. Finally, a single dose of 3 mg CC-122 was safe and well tolerated by healthy subjects and subjects with mild, moderate, and severe renal impairment.

Keywords: CC-122; avadomide; pharmacokinetics; renal impairment; safety; tolerability.

Publication types

  • Clinical Trial, Phase I
  • Multicenter Study
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adaptor Proteins, Signal Transducing / drug effects
  • Adaptor Proteins, Signal Transducing / metabolism
  • Adult
  • Aged
  • Carcinoma, Hepatocellular / drug therapy
  • Case-Control Studies
  • Cytochrome P-450 CYP1A2 Inhibitors / administration & dosage
  • Cytochrome P-450 CYP1A2 Inhibitors / adverse effects
  • Cytochrome P-450 CYP1A2 Inhibitors / pharmacokinetics
  • Cytochrome P-450 CYP3A Inhibitors / administration & dosage
  • Cytochrome P-450 CYP3A Inhibitors / adverse effects
  • Cytochrome P-450 CYP3A Inhibitors / pharmacokinetics
  • Dose-Response Relationship, Drug
  • Drug Interactions
  • Female
  • Genetic Pleiotropy / drug effects*
  • Genetic Pleiotropy / genetics
  • Glioblastoma / drug therapy
  • Hematologic Neoplasms / drug therapy*
  • Humans
  • Liver Neoplasms / pathology
  • Male
  • Middle Aged
  • Piperidones / administration & dosage
  • Piperidones / adverse effects
  • Piperidones / pharmacokinetics*
  • Piperidones / pharmacology
  • Quinazolinones / administration & dosage
  • Quinazolinones / adverse effects
  • Quinazolinones / pharmacokinetics*
  • Quinazolinones / pharmacology
  • Renal Insufficiency / blood*
  • Renal Insufficiency / ethnology
  • Renal Insufficiency / metabolism
  • Renal Insufficiency / urine
  • Safety
  • Severity of Illness Index
  • Ubiquitin-Protein Ligases / drug effects
  • Ubiquitin-Protein Ligases / metabolism

Substances

  • 3-(5-amino-2-methyl-4-oxoquinazolin-3(4H)-yl)piperidine-2,6-dione
  • Adaptor Proteins, Signal Transducing
  • CRBN protein, human
  • Cytochrome P-450 CYP1A2 Inhibitors
  • Cytochrome P-450 CYP3A Inhibitors
  • Piperidones
  • Quinazolinones
  • Ubiquitin-Protein Ligases