Real-world evidence in cystic fibrosis modulator development: Establishing a path forward

J Cyst Fibros. 2020 May;19(3):e11-e12. doi: 10.1016/j.jcf.2020.03.020. Epub 2020 Apr 11.

¹ Departments of Biostatistics and Pediatrics, Seattle Children's Research Institute, University of Washington, Seattle, WA, USA. Electronic address: amag@uw.edu.
² Department of Epidemiology, Seattle Children's Research Institute, University of Washington, Seattle, WA, USA.
³ Department of Biostatistics, Seattle Children's Research Institute, University of Washington, Seattle, WA, USA.
⁴ Department of Pediatrics, Seattle Children's Research Institute, University of Washington, Seattle, WA, USA.
⁵ Departments of Biostatistics and Pediatrics, Seattle Children's Research Institute, University of Washington, Seattle, WA, USA.

No abstract available

Keywords: clinical trial; historical controls; real-world evidence.

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