Management of Hyperhemolysis in β-thalassemia With Multiple Immunosuppressives, Including Complement Blockade

J Pediatr Hematol Oncol. 2021 Nov 1;43(8):e1145-e1147. doi: 10.1097/MPH.0000000000002059.

Abstract

Hyperhemolysis is a life-threatening condition of exaggerated hemolysis of red blood cells which occurs in patients receiving chronic transfusion therapy. We present a 19-year-old male with the β-thalassemia major with an episode of hyperhemolysis. Hemolysis was initially unresponsive to immunosuppression but responded after the addition of eculizumab. Several weeks after stabilization, hemolysis returned; which was also managed with immunosuppression and eculizumab. Hyperhemolysis presents significant challenges in β-thalassemia due to the underlying dysfunctional erythropoiesis and transfusion dependence. Aggressive immunosuppression combined with eculizumab successfully slowed the hemolysis and allowed for the resumption of transfusions.

Publication types

  • Case Reports

MeSH terms

  • Adult
  • Antibodies, Monoclonal, Humanized / therapeutic use*
  • Complement Inactivating Agents / therapeutic use*
  • Drug Therapy, Combination
  • Hematologic Diseases / drug therapy*
  • Hematologic Diseases / etiology
  • Hematologic Diseases / pathology
  • Hemolysis / drug effects*
  • Humans
  • Immunosuppressive Agents / therapeutic use*
  • Male
  • Prognosis
  • Young Adult
  • beta-Thalassemia / complications*

Substances

  • Antibodies, Monoclonal, Humanized
  • Complement Inactivating Agents
  • Immunosuppressive Agents
  • eculizumab