Pharmacokinetics and safety of niraparib in patients with moderate hepatic impairment

Cancer Chemother Pharmacol. 2021 Nov;88(5):825-836. doi: 10.1007/s00280-021-04329-8. Epub 2021 Jul 29.

Abstract

Purpose: The purpose of this study is to characterize niraparib pharmacokinetics (PK) and safety in patients with normal hepatic function (NHF) versus moderate hepatic impairment (MHI).

Methods: Patients with advanced solid tumors were stratified by NHF or MHI (National Cancer Institute-Organ Dysfunction Working Group criteria [bilirubin > 1.5-3 × upper limit of normal and any aspartate aminotransferase elevation]). In the PK phase, all patients received one 300 mg dose of niraparib. In the extension phase, patients with MHI received niraparib 200 mg daily; patients with NHF received 200 or 300 mg based on weight (< 77 kg, ≥ 77 kg)/platelets (< 150,000/µL, ≥ 150,000/µL). PK parameters included maximum concentration (Cmax), area under the curve to last measured concentration (AUClast) and extrapolated to infinity (AUCinf). Safety was assessed in both phases. Exposure-response (E-R) modeling was used to predict MHI effects on exposure and safety of niraparib doses ≤ 200 mg or 300/200 mg or 200/100 mg weight/platelet regimens.

Results: In the PK phase (NHF, n = 9; MHI, n = 8), mean niraparib Cmax was 7% lower in patients with MHI versus NHF. Mean exposure (AUClast, AUCinf) was increased by 45% and 56%, respectively, in patients with MHI without impacting tolerability. In the extension phase (NHF, n = 8; MHI, n = 7), the overall safety profile was consistent with previous trials. In patients with MHI, E-R modeling predicted niraparib 200 mg reduced Grade ≥ 3 thrombocytopenia incidence, whereas a 200/100 mg regimen yielded exposures below efficacy-associated levels in 15% of patients.

Conclusion: These findings support adjusting the 300 mg niraparib starting dose to 200 mg QD in patients with MHI.

Trial registration: NCT03359850; registered December 2, 2017.

Keywords: Dosing; Hepatic impairment; Niraparib; Pharmacokinetics; Safety.

Publication types

  • Clinical Trial, Phase I
  • Multicenter Study
  • Research Support, N.I.H., Extramural
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Aged
  • Area Under Curve
  • Dose-Response Relationship, Drug
  • Female
  • Humans
  • Indazoles / administration & dosage
  • Indazoles / adverse effects*
  • Indazoles / blood
  • Indazoles / pharmacokinetics*
  • Liver / drug effects*
  • Liver / physiopathology
  • Male
  • Middle Aged
  • Piperidines / administration & dosage
  • Piperidines / adverse effects*
  • Piperidines / blood
  • Piperidines / pharmacokinetics*

Substances

  • Indazoles
  • Piperidines
  • niraparib

Associated data

  • ClinicalTrials.gov/NCT03359850