Effect of hydroxyurea therapy on intravascular hemolysis and endothelial dysfunction markers in sickle cell anemia patients

Ann Hematol. 2021 Nov;100(11):2669-2676. doi: 10.1007/s00277-021-04636-3. Epub 2021 Aug 28.

Abstract

Intravascular hemolysis (IH) contributes to the development of endothelial dysfunction (ED) in sickle cell anemia (SCA), and the effects of hydroxyurea (HU, the only approved drug that decreases the frequency and severity of vaso-oclussive crises) on IH and ED in SCA remain unclear. We evaluated and compared the markers of IH among steady-state adult Brazilians with SCA and HbAA individuals. Overall, this cross-sectional study enrolled 30 SCA patients not receiving HU therapy (HbSS), 25 SCA patients receiving HU therapy (HbSS_HU), and 32 HbAA volunteers (HbAA). The IH markers evaluated were serum Lactate Dehydrogenase (LDH), total heme, plasma hemoglobin (pHb), and soluble CD163 (sCD163). The ED markers analyzed were plasma von Willebrand factor (VWF:Ag), VWF ristocetin cofactor activity (VWF:RCo) levels, antigen of VWF-cleaving protease (ADAMTS13:Ag), thrombospondin-1, endothelin-1 levels, and ADAMTS13 Activity (ADAMTS13:Act). The levels of VWF:Ag, VWF:RCo, total heme, thrombospondin-1, and endothelin-1 were significantly higher in SCA patients (HbSS and HbSS_HU) compared to HbAA individuals. Also, pHb, LDH, and thrombospondin-1 levels were significantly higher in the HbSS group than in the HbSS_HU group. Contrarily, the levels of sCD163, ADAMTS13:Ag, and ADAMTS13:Act were significantly lower in both groups of SCA patients than HbAA controls, and ADAMTS13:Act levels were significantly lower in HbSS compared to HbSS_HU patients. The higher ADAMTS13 activity levels in those on HU therapy may be attributed to lower pHb and thrombospondin-1 levels as previously shown by in vitro studies that thrombospondin-1 and pHb are bound to VWF. Thus, VWF is restrained from ADAMTS13 activity and cleavage.

Keywords: Brazilian population; Endothelial dysfunction; Hydroxyurea; Intravascular hemolysis; Sickle cell anemia.

Publication types

  • Comparative Study

MeSH terms

  • ADAMTS13 Protein / blood
  • Adolescent
  • Adult
  • Anemia, Sickle Cell / blood
  • Anemia, Sickle Cell / drug therapy*
  • Antigens, CD / blood
  • Antigens, Differentiation, Myelomonocytic / blood
  • Biomarkers
  • Cross-Sectional Studies
  • Endothelium, Vascular / drug effects
  • Endothelium, Vascular / physiopathology*
  • Female
  • Heme / analysis
  • Hemoglobins / analysis
  • Hemolysis / drug effects*
  • Humans
  • Hydroxyurea / pharmacology
  • Hydroxyurea / therapeutic use*
  • L-Lactate Dehydrogenase / blood
  • Male
  • Middle Aged
  • Prohibitins
  • Receptors, Cell Surface / blood
  • Thrombospondin 1 / blood
  • Young Adult
  • von Willebrand Factor / analysis

Substances

  • Antigens, CD
  • Antigens, Differentiation, Myelomonocytic
  • Biomarkers
  • CD163 antigen
  • Hemoglobins
  • PHB protein, human
  • Prohibitins
  • Receptors, Cell Surface
  • Thrombospondin 1
  • von Willebrand Factor
  • Heme
  • L-Lactate Dehydrogenase
  • ADAMTS13 Protein
  • ADAMTS13 protein, human
  • Hydroxyurea