Plasmid-Based Donor Templates for Nonviral CRISPR/Cas9-Mediated Gene Knock-In in Human T Cells

Curr Protoc. 2022 Sep;2(9):e538. doi: 10.1002/cpz1.538.

Abstract

Effective and precise gene editing of T lymphocytes is critical for advancing the understanding of T cell biology and the development of next-generation cellular therapies. Although methods for effective CRISPR/Cas9-mediated gene knock-out in primary human T cells have been developed, complementary techniques for nonviral gene knock-in can be cumbersome and inefficient. Here, we report a simple and efficient method for nonviral CRISPR/Cas9-based gene knock-in utilizing plasmid-based donor DNA templates. © 2022 Wiley Periodicals LLC. Basic Protocol 1: Purification of human CD4+ or CD8+ T cells from blood Basic Protocol 2: Activation of purified CD4+ or CD8+ T cells using TransAct CD3/CD28 agonist-conjugated nanomatrix Basic Protocol 3: Preparation of Cas9/sgRNA RNPs Basic Protocol 4: Transfection of CAS9-RNP and knock-in template into human T cells Support Protocol 1: Purity check following magnetic T cell isolation Support Protocol 2: Dextramer staining of TCR-edited T cells Support Protocol 3: Functional characterization of TCR knock-in T cells Support Protocol 4: Detection of knock-in reporter activity in CRISPR/CAS9-edited T cells.

Keywords: CRISPR; Cas9; T cell; cell therapy; gene engineering; knock-in; lymphocyte.

MeSH terms

  • CD28 Antigens / genetics
  • CD8-Positive T-Lymphocytes* / metabolism
  • CRISPR-Cas Systems* / genetics
  • DNA
  • Gene Knock-In Techniques
  • Humans
  • Plasmids / genetics
  • Receptors, Antigen, T-Cell / genetics
  • Ribonucleoproteins / genetics

Substances

  • CD28 Antigens
  • Receptors, Antigen, T-Cell
  • Ribonucleoproteins
  • DNA