A CRISPR-Cas Cure for HIV/AIDS

Int J Mol Sci. 2023 Jan 13;24(2):1563. doi: 10.3390/ijms24021563.

Abstract

Human immunodeficiency virus (HIV) infections and HIV-induced acquired immunodeficiency syndrome (AIDS) continue to represent a global health burden. There is currently no effective vaccine, nor any cure, for HIV infections; existing antiretroviral therapy can suppress viral replication, but only as long as antiviral drugs are taken. HIV infects cells of the host immune system, and it can establish a long-lived viral reservoir, which can be targeted and edited through gene therapy. Gene editing platforms based on the clustered regularly interspaced palindromic repeat-Cas system (CRISPR-Cas) have been recognized as promising tools in the development of gene therapies for HIV infections. In this review, we evaluate the current landscape of CRISPR-Cas-based therapies against HIV, with an emphasis on the infection biology of the virus as well as the activity of host restriction factors. We discuss the potential of a combined CRISPR-Cas approach that targets host and viral genes to activate antiviral host factors and inhibit viral replication simultaneously. Lastly, we focus on the challenges and potential solutions of CRISPR-Cas gene editing approaches in achieving an HIV cure.

Keywords: CRISPR-Cas; HIV; host factors; viral genes.

Publication types

  • Review

MeSH terms

  • Acquired Immunodeficiency Syndrome* / genetics
  • Acquired Immunodeficiency Syndrome* / therapy
  • Antiviral Agents
  • CRISPR-Cas Systems / genetics
  • Gene Editing
  • HIV Infections* / genetics
  • HIV Infections* / therapy
  • Humans
  • Viruses*

Substances

  • Antiviral Agents