Daratumumab Plus Bortezomib and Dexamethasone in Newly Diagnosed Systemic Light Chain Amyloidosis

Curr Probl Cancer. 2023 Jun;47(3):100953. doi: 10.1016/j.currproblcancer.2023.100953. Epub 2023 Feb 14.

Abstract

Light chain amyloidosis (AL) is a plasma cell dyscrasia characterized by organ dysfunction, morbidity, and early mortality. Daratumumab in combination with cyclophosphamide, bortezomib, and dexamethasone is now standard frontline AL therapy; however, not all patients are candidates for this intensive regimen. Given the potency of Daratumumab, we evaluated an alternative frontline regimen: daratumumab, bortezomib, and limited-duration dexamethasone (Dara-Vd). Over a 3 year period, we treated 21 patients with Dara-Vd. At baseline, all patients had cardiac and/or renal dysfunction, including 30% of patients with Mayo stage IIIB cardiac disease. Nineteen of 21 patients (90%) achieved a hematologic response with 38% achieving a complete response. The median time to response was 11 days. Ten of 15 (67%) evaluable patients achieved a cardiac response and 7 of 9 (78%) achieved a renal response. The 1-year overall survival was 76%. In untreated systemic AL amyloidosis, Dara-Vd produces rapid and deep hematologic and organ responses. Dara-Vd was well-tolerated and efficacious, even among patients with extensive cardiac dysfunction.

Keywords: Amyloidosis; Daratumumab; Induction.

MeSH terms

  • Amyloidosis* / drug therapy
  • Antineoplastic Combined Chemotherapy Protocols / therapeutic use
  • Bortezomib
  • Dexamethasone / therapeutic use
  • Heart Diseases* / chemically induced
  • Humans
  • Immunoglobulin Light-chain Amyloidosis* / drug therapy
  • Treatment Outcome

Substances

  • Bortezomib
  • daratumumab
  • Dexamethasone