Efficacy of hyperthermic intraperitoneal chemotherapy in colorectal cancer: A phase I and III open label randomized controlled registry-based clinical trial protocol

PLoS One. 2024 Mar 4;19(3):e0294018. doi: 10.1371/journal.pone.0294018. eCollection 2024.

Abstract

Standard treatment for patient with peritoneal metastases from colorectal cancer is cytoreductive surgery (CRS) and hyperthermic intraperitoneal chemotherapy (HIPEC). In recent years, the efficacy of oxaliplatin-based HIPEC has been challenged. An intensified HIPEC (oxaliplatin+irinotecan) in combination with early postoperative intraperitoneal chemotherapy (EPIC) has shown increased recurrence-free survival in retrospective studies. The aim of this trial is to develop a new HIPEC/EPIC regimen and evaluate its effect on morbidity, oncological outcome, and quality-of-life (QoL). This study is designed as a combined phase I/III multicenter randomized trial (RCT) of patients with peritoneal metastases from colorectal cancer eligible for CRS-HIPEC. An initial phase I dose escalation study, designed as a 3+3 stepwise escalation, will determine the maximum tolerable dose of 5-Fluorouracil (5-FU) as 1-day EPIC, enrolling a total of 15-30 patients in 5 dose levels. In the phase III efficacy study, patients are randomly assigned intraoperatively to either the standard treatment with oxaliplatin HIPEC (control arm) or oxaliplatin/irinotecan-HIPEC in combination with single dose of 1-day 5-FU EPIC (experimental arm). 5-FU is administered intraoperatively after CRS-HIPEC and closure of the abdomen. The primary endpoint is 12-month recurrence-free survival. Secondary endpoints include 5-year overall survival, 5-year recurrence-free survival (registry based), postoperative complications, and QoL up to 3 years after study treatment. This phase I/III trial aims to identify a more effective treatment of colorectal peritoneal metastases by combination of HIPEC and EPIC.

Publication types

  • Clinical Trial Protocol

MeSH terms

  • Clinical Trials, Phase I as Topic
  • Clinical Trials, Phase III as Topic
  • Colorectal Neoplasms* / drug therapy
  • Fluorouracil / therapeutic use
  • Humans
  • Hyperthermic Intraperitoneal Chemotherapy
  • Irinotecan
  • Multicenter Studies as Topic
  • Oxaliplatin / therapeutic use
  • Peritoneal Neoplasms* / drug therapy
  • Quality of Life
  • Randomized Controlled Trials as Topic
  • Registries
  • Retrospective Studies

Substances

  • Fluorouracil
  • Irinotecan
  • Oxaliplatin

Grants and funding

Complete funding has been achieved through the Swedish Research Council. The funders had no role in study design, data collection and analysis, decision to publish, or preparation of the manuscript. None of the authors have received any salary from the funder.