Neurocognitive assessment platform for clinical trials in PKU: White paper developed by the NPKUA neurocognitive workgroup

Mol Genet Metab. 2024 Sep-Oct;143(1-2):108555. doi: 10.1016/j.ymgme.2024.108555. Epub 2024 Jul 25.
No abstract available

Keywords: Clinical trials; Functional outcomes; Neuropsychological outcomes; PKU; Phenylketonuria.

Publication types

  • Editorial

MeSH terms

  • Child
  • Clinical Trials as Topic*
  • Cognition
  • Humans
  • Neuropsychological Tests
  • Phenylketonurias* / diagnosis