Sestrin2 drives ER-phagy in response to protein misfolding

Dev Cell. 2024 Aug 19;59(16):2035-2052.e10. doi: 10.1016/j.devcel.2024.07.004. Epub 2024 Aug 1.

Abstract

Protein biogenesis within the endoplasmic reticulum (ER) is crucial for organismal function. Errors during protein folding necessitate the removal of faulty products. ER-associated protein degradation and ER-phagy target misfolded proteins for proteasomal and lysosomal degradation. The mechanisms initiating ER-phagy in response to ER proteostasis defects are not well understood. By studying mouse primary cells and patient samples as a model of ER storage disorders (ERSDs), we show that accumulation of faulty products within the ER triggers a response involving SESTRIN2, a nutrient sensor controlling mTORC1 signaling. SESTRIN2 induction by XBP1 inhibits mTORC1's phosphorylation of TFEB/TFE3, allowing these transcription factors to enter the nucleus and upregulate the ER-phagy receptor FAM134B along with lysosomal genes. This response promotes ER-phagy of misfolded proteins via FAM134B-Calnexin complex. Pharmacological induction of FAM134B improves clearance of misfolded proteins in ERSDs. Our study identifies the interplay between nutrient signaling and ER quality control, suggesting therapeutic strategies for ERSDs.

Keywords: ER storage disorders; ER-phagy; FAM134B; TFEB; alpha(1)-antitrypsin Z (alpha(1)-ATZ); autophagy; collagen; endoplasmic reticulum; mTORC1; quality control.

MeSH terms

  • Animals
  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors
  • Endoplasmic Reticulum Stress
  • Endoplasmic Reticulum* / metabolism
  • Humans
  • Intracellular Signaling Peptides and Proteins / genetics
  • Intracellular Signaling Peptides and Proteins / metabolism
  • Lysosomes / metabolism
  • Mechanistic Target of Rapamycin Complex 1* / metabolism
  • Membrane Proteins / genetics
  • Membrane Proteins / metabolism
  • Mice
  • Nuclear Proteins / genetics
  • Nuclear Proteins / metabolism
  • Phosphorylation
  • Protein Folding*
  • Proteostasis
  • Sestrins / genetics
  • Sestrins / metabolism
  • Signal Transduction
  • X-Box Binding Protein 1* / genetics
  • X-Box Binding Protein 1* / metabolism

Substances

  • Mechanistic Target of Rapamycin Complex 1
  • Sesn2 protein, mouse
  • X-Box Binding Protein 1
  • Membrane Proteins
  • Intracellular Signaling Peptides and Proteins
  • SESN2 protein, human
  • Fam134b protein, mouse
  • Nuclear Proteins
  • Xbp1 protein, mouse
  • Sestrins
  • RETREG1 protein, human
  • Tcfeb protein, mouse
  • Basic Helix-Loop-Helix Leucine Zipper Transcription Factors