Zanubrutinib plus R-CHOP for the treatment of newly diagnosed double-expressor lymphoma: A phase 2 clinical study

Cancer. 2025 Jan 1;131(1):e35697. doi: 10.1002/cncr.35697.

Abstract

Background: Double-expressor lymphoma (DEL) has a poorer prognosis than other subtypes of diffuse large B-cell lymphoma (DLBCL). This study is a multicenter, prospective, single-arm, phase 2 clinical study initiated by investigators to evaluate the efficacy and safety of combined zanubrutinib with R-CHOP, which includes rituximab, cyclophosphamide, doxorubicin, vincristine, and prednisone for patients with DEL (stage II or more), as well as to explore factors related to efficacy preliminarily.

Methods: From November 2020 to July 2022, 48 newly diagnosed patients were enrolled. All patients received twice-daily oral zanubrutinib (160 mg) for 6 months and standardized R-CHOP regimen for six to eight cycles.

Results: The objective response rate (ORR) was 89.6%, with a complete response rate (CRR) of 83.3%. The median follow-up was 29.3 months. The median progression-free survival (PFS) and overall survival (OS) were not reached. The PFS and OS were 81.25% and 93.75% at 2 years, respectively. Grade ≥3 adverse events (AEs) were reported in 23 of 48 (47.9%) patients. Next-generation sequencing (NGS) results of 33 patients showed that TP53, MYD88, and PIM1 were the most common mutated gene. Multivariate analysis revealed that BCL-6 gene rearrangement was an adverse prognostic factor for both PFS (hazard ratio [HR], 0.247; 95% confidence article [CI], 0.068-0.9; p = .034) and OS (HR, 0.057; 95% CI, 0.006-0.591; p = .016), whereas the number of extranodal involvements also significantly influenced OS (HR, 15.12; 95% CI, 1.07-213.65; p = .044).

Conclusions: Zanubrutinib in combination with R-CHOP is an effective option for DEL patients, and the toxicity of zanubrutinib is entirely acceptable for patients.

Keywords: BCL2; BTKi; MYC; double‐expressor lymphoma; zanubrutinib.

Publication types

  • Clinical Trial, Phase II
  • Multicenter Study

MeSH terms

  • Adult
  • Aged
  • Antineoplastic Combined Chemotherapy Protocols* / therapeutic use
  • Cyclophosphamide* / administration & dosage
  • Cyclophosphamide* / adverse effects
  • Cyclophosphamide* / therapeutic use
  • Doxorubicin* / administration & dosage
  • Doxorubicin* / adverse effects
  • Doxorubicin* / therapeutic use
  • Female
  • Humans
  • Lymphoma, Large B-Cell, Diffuse* / drug therapy
  • Lymphoma, Large B-Cell, Diffuse* / genetics
  • Lymphoma, Large B-Cell, Diffuse* / pathology
  • Male
  • Middle Aged
  • Myeloid Differentiation Factor 88 / genetics
  • Piperidines / administration & dosage
  • Piperidines / adverse effects
  • Piperidines / therapeutic use
  • Prednisone* / administration & dosage
  • Prednisone* / adverse effects
  • Prednisone* / therapeutic use
  • Progression-Free Survival
  • Prospective Studies
  • Proto-Oncogene Proteins c-bcl-6 / genetics
  • Pyrazoles* / administration & dosage
  • Pyrazoles* / adverse effects
  • Pyrazoles* / therapeutic use
  • Pyrimidines / administration & dosage
  • Pyrimidines / adverse effects
  • Pyrimidines / therapeutic use
  • Rituximab* / administration & dosage
  • Rituximab* / adverse effects
  • Tumor Suppressor Protein p53 / genetics
  • Vincristine* / administration & dosage
  • Vincristine* / adverse effects
  • Vincristine* / therapeutic use

Substances

  • Cyclophosphamide
  • Rituximab
  • Vincristine
  • zanubrutinib
  • Doxorubicin
  • Prednisone
  • Pyrazoles
  • R-CHOP protocol
  • Pyrimidines
  • MYD88 protein, human
  • Proto-Oncogene Proteins c-bcl-6
  • Myeloid Differentiation Factor 88
  • BCL6 protein, human
  • Piperidines
  • Tumor Suppressor Protein p53
  • TP53 protein, human