Linkage and mutation analysis in an extended family with Charcot-Marie-Tooth disease type 1B

J Med Genet. 1994 Oct;31(10):811-5. doi: 10.1136/jmg.31.10.811.

Abstract

Charcot-Marie-Tooth disease type 1 (CMT1) or hereditary motor and sensory neuropathy type I (HMSNI) is an autosomal dominant peripheral neuropathy. In most families the disease segregates with a 1.5 Mb duplication on chromosome 17p11.2 (CMT1A). A few patients have been found with point mutations in the PMP-22 gene. In some families linkage has been found with markers located on chromosome 1q21-q25 (CMT1B) and more recently mutations have been identified in the P0 gene. We analysed an extended CMT1 pedigree (CMT-B) without the CMT1A duplication. Significant positive linkage with chromosome 1 indicated that this family is of the CMT1B subtype. Sequencing of the candidate gene P0 located in chromosome band 1q21-q23 showed a C to A point mutation at position 446 in exon 3 resulting in an Asp134Glu substitution. Since the P0 mutation cosegregated with CMT1 disease we suggest that this mutation is the primary genetic cause of CMT1B in family CMT-B.

Publication types

  • Case Reports
  • Research Support, Non-U.S. Gov't

MeSH terms

  • Adult
  • Base Sequence
  • Blotting, Southern
  • Cell Adhesion Molecules, Neuronal / genetics
  • Charcot-Marie-Tooth Disease / genetics*
  • Chromosome Mapping
  • Chromosomes, Human, Pair 1*
  • Chromosomes, Human, Pair 17
  • DNA / genetics*
  • DNA Mutational Analysis
  • DNA Primers
  • Exons
  • Female
  • Humans
  • Male
  • Molecular Sequence Data
  • Myelin P0 Protein
  • Myelin Proteins / genetics
  • Pedigree
  • Point Mutation
  • Polymerase Chain Reaction

Substances

  • Cell Adhesion Molecules, Neuronal
  • DNA Primers
  • Myelin P0 Protein
  • Myelin Proteins
  • PMP22 protein, human
  • DNA