Neoplastic reversion accomplished by high efficiency adenoviral-mediated delivery of an anti-ras ribozyme

Cancer Res. 1995 May 15;55(10):2024-8.

Abstract

Strategies have been developed to abrogate the aberrant expression of dominant oncogenes as a means to accomplish targeted tumor eradication. We have demonstrated previously the utility of this approach using a hammerhead ribozyme designed to cleave the mutant sequence in codon 12 of the activated H-ras oncogene transcript. To develop this strategy into a practical means to approach malignant disease, methods must be developed to accomplish high efficiency delivery of the ribozyme to target neoplastic cells. To accomplish this, a recombinant adenovirus was designed that encoded a gene cassette for the H-ras ribozyme. By using this virus, it was possible to accomplish high efficiency reversion of the neoplastic phenotype in mutant H-ras expressing tumor cells without the need for any selection steps. The demonstration of the utility of adenoviral-mediated delivery of anticancer ribozymes will allow the practical development of gene therapy strategies on this basis.

MeSH terms

  • Adenoviridae / enzymology
  • Adenoviridae / genetics
  • Animals
  • Base Sequence
  • Cell Division / genetics
  • Codon / genetics
  • Genes, ras / genetics*
  • Genetic Therapy / methods*
  • Genetic Vectors / administration & dosage
  • Genetic Vectors / genetics*
  • Humans
  • Mice
  • Mice, Inbred BALB C
  • Mice, Nude
  • Molecular Sequence Data
  • RNA, Catalytic / administration & dosage*
  • RNA, Catalytic / genetics
  • Transfection / genetics
  • Transfection / methods
  • Tumor Cells, Cultured
  • Urinary Bladder Neoplasms / pathology
  • Urinary Bladder Neoplasms / therapy

Substances

  • Codon
  • RNA, Catalytic