Urbinati F - Search Results

1

A novel human gamma-globin gene vector for genetic correction of sickle cell anemia in a humanized sickle mouse model: critical determinants for successful correction.

Perumbeti A, Higashimoto T, Urbinati F, Franco R, Meiselman HJ, Witte D, Malik P. Perumbeti A, et al. Among authors: urbinati f. Blood. 2009 Aug 6;114(6):1174-85. doi: 10.1182/blood-2009-01-201863. Epub 2009 May 27. Blood. 2009. PMID: 19474450 Free PMC article.

2

Mechanism of reduction in titers from lentivirus vectors carrying large inserts in the 3'LTR.

Urbinati F, Arumugam P, Higashimoto T, Perumbeti A, Mitts K, Xia P, Malik P. Urbinati F, et al. Mol Ther. 2009 Sep;17(9):1527-36. doi: 10.1038/mt.2009.89. Epub 2009 Apr 21. Mol Ther. 2009. PMID: 19384292 Free PMC article.

3

Genotoxic potential of lineage-specific lentivirus vectors carrying the beta-globin locus control region.

Arumugam PI, Higashimoto T, Urbinati F, Modlich U, Nestheide S, Xia P, Fox C, Corsinotti A, Baum C, Malik P. Arumugam PI, et al. Among authors: urbinati f. Mol Ther. 2009 Nov;17(11):1929-37. doi: 10.1038/mt.2009.183. Epub 2009 Aug 25. Mol Ther. 2009. PMID: 19707188 Free PMC article.

4

The 3' region of the chicken hypersensitive site-4 insulator has properties similar to its core and is required for full insulator activity.

Arumugam PI, Urbinati F, Velu CS, Higashimoto T, Grimes HL, Malik P. Arumugam PI, et al. Among authors: urbinati f. PLoS One. 2009 Sep 10;4(9):e6995. doi: 10.1371/journal.pone.0006995. PLoS One. 2009. PMID: 19746166 Free PMC article.

5

The woodchuck hepatitis virus post-transcriptional regulatory element reduces readthrough transcription from retroviral vectors.

Higashimoto T, Urbinati F, Perumbeti A, Jiang G, Zarzuela A, Chang LJ, Kohn DB, Malik P. Higashimoto T, et al. Among authors: urbinati f. Gene Ther. 2007 Sep;14(17):1298-304. doi: 10.1038/sj.gt.3302979. Epub 2007 Jun 28. Gene Ther. 2007. PMID: 17597793

6

Pathophysiology and therapy for haemoglobinopathies. Part II: thalassaemias.

Urbinati F, Madigan C, Malik P. Urbinati F, et al. Expert Rev Mol Med. 2006 May 9;8(10):1-26. doi: 10.1017/S1462399406010805. Expert Rev Mol Med. 2006. PMID: 16684395 Review.

7

Correction of the sickle cell disease mutation in human hematopoietic stem/progenitor cells.

Hoban MD, Cost GJ, Mendel MC, Romero Z, Kaufman ML, Joglekar AV, Ho M, Lumaquin D, Gray D, Lill GR, Cooper AR, Urbinati F, Senadheera S, Zhu A, Liu PQ, Paschon DE, Zhang L, Rebar EJ, Wilber A, Wang X, Gregory PD, Holmes MC, Reik A, Hollis RP, Kohn DB. Hoban MD, et al. Among authors: urbinati f. Blood. 2015 Apr 23;125(17):2597-604. doi: 10.1182/blood-2014-12-615948. Epub 2015 Mar 2. Blood. 2015. PMID: 25733580 Free PMC article.

8

β-globin gene transfer to human bone marrow for sickle cell disease.

Romero Z, Urbinati F, Geiger S, Cooper AR, Wherley J, Kaufman ML, Hollis RP, de Assin RR, Senadheera S, Sahagian A, Jin X, Gellis A, Wang X, Gjertson D, Deoliveira S, Kempert P, Shupien S, Abdel-Azim H, Walters MC, Meiselman HJ, Wenby RB, Gruber T, Marder V, Coates TD, Kohn DB. Romero Z, et al. Among authors: urbinati f. J Clin Invest. 2013 Jul 1;123(8):3317-30. doi: 10.1172/JCI67930. Online ahead of print. J Clin Invest. 2013. PMID: 23863630 Free PMC article.

9

Potentially therapeutic levels of anti-sickling globin gene expression following lentivirus-mediated gene transfer in sickle cell disease bone marrow CD34+ cells.

Urbinati F, Hargrove PW, Geiger S, Romero Z, Wherley J, Kaufman ML, Hollis RP, Chambers CB, Persons DA, Kohn DB, Wilber A. Urbinati F, et al. Exp Hematol. 2015 May;43(5):346-351. doi: 10.1016/j.exphem.2015.01.009. Epub 2015 Feb 12. Exp Hematol. 2015. PMID: 25681747 Free PMC article.

10

Preclinical studies for a phase 1 clinical trial of autologous hematopoietic stem cell gene therapy for sickle cell disease.

Urbinati F, Wherley J, Geiger S, Fernandez BC, Kaufman ML, Cooper A, Romero Z, Marchioni F, Reeves L, Read E, Nowicki B, Grassman E, Viswanathan S, Wang X, Hollis RP, Kohn DB. Urbinati F, et al. Cytotherapy. 2017 Sep;19(9):1096-1112. doi: 10.1016/j.jcyt.2017.06.002. Epub 2017 Jul 18. Cytotherapy. 2017. PMID: 28733131

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