McCarty DM - Search Results

1

Mucopolysaccharidosis IIIB, a lysosomal storage disease, triggers a pathogenic CNS autoimmune response.

Killedar S, Dirosario J, Divers E, Popovich PG, McCarty DM, Fu H. Killedar S, et al. Among authors: mccarty dm. J Neuroinflammation. 2010 Jul 16;7:39. doi: 10.1186/1742-2094-7-39. J Neuroinflammation. 2010. PMID: 20637096 Free PMC article.

2

Restoration of central nervous system alpha-N-acetylglucosaminidase activity and therapeutic benefits in mucopolysaccharidosis IIIB mice by a single intracisternal recombinant adeno-associated viral type 2 vector delivery.

Fu H, DiRosario J, Kang L, Muenzer J, McCarty DM. Fu H, et al. Among authors: mccarty dm. J Gene Med. 2010 Jul;12(7):624-33. doi: 10.1002/jgm.1480. J Gene Med. 2010. PMID: 20603889

3

Differential distribution of heparan sulfate glycoforms and elevated expression of heparan sulfate biosynthetic enzyme genes in the brain of mucopolysaccharidosis IIIB mice.

McCarty DM, DiRosario J, Gulaid K, Killedar S, Oosterhof A, van Kuppevelt TH, Martin PT, Fu H. McCarty DM, et al. Metab Brain Dis. 2011 Mar;26(1):9-19. doi: 10.1007/s11011-010-9230-x. Epub 2011 Jan 12. Metab Brain Dis. 2011. PMID: 21225451 Free PMC article.

4

Correction of neurological disease of mucopolysaccharidosis IIIB in adult mice by rAAV9 trans-blood-brain barrier gene delivery.

Fu H, Dirosario J, Killedar S, Zaraspe K, McCarty DM. Fu H, et al. Among authors: mccarty dm. Mol Ther. 2011 Jun;19(6):1025-33. doi: 10.1038/mt.2011.34. Epub 2011 Mar 8. Mol Ther. 2011. PMID: 21386820 Free PMC article.

5

Innate and adaptive immune activation in the brain of MPS IIIB mouse model.

DiRosario J, Divers E, Wang C, Etter J, Charrier A, Jukkola P, Auer H, Best V, Newsom DL, McCarty DM, Fu H. DiRosario J, et al. Among authors: mccarty dm. J Neurosci Res. 2009 Mar;87(4):978-90. doi: 10.1002/jnr.21912. J Neurosci Res. 2009. PMID: 18951493

6

Peripheral nervous system neuropathology and progressive sensory impairments in a mouse model of Mucopolysaccharidosis IIIB.

Fu H, Bartz JD, Stephens RL Jr, McCarty DM. Fu H, et al. Among authors: mccarty dm. PLoS One. 2012;7(9):e45992. doi: 10.1371/journal.pone.0045992. Epub 2012 Sep 25. PLoS One. 2012. PMID: 23049915 Free PMC article.

7

Amyloidosis, synucleinopathy, and prion encephalopathy in a neuropathic lysosomal storage disease: the CNS-biomarker potential of peripheral blood.

Naughton BJ, Duncan FJ, Murrey D, Ware T, Meadows A, McCarty DM, Fu H. Naughton BJ, et al. Among authors: mccarty dm. PLoS One. 2013 Nov 21;8(11):e80142. doi: 10.1371/journal.pone.0080142. eCollection 2013. PLoS One. 2013. PMID: 24278249 Free PMC article.

8

Significantly increased lifespan and improved behavioral performances by rAAV gene delivery in adult mucopolysaccharidosis IIIB mice.

Fu H, Kang L, Jennings JS, Moy SS, Perez A, Dirosario J, McCarty DM, Muenzer J. Fu H, et al. Among authors: mccarty dm. Gene Ther. 2007 Jul;14(14):1065-77. doi: 10.1038/sj.gt.3302961. Epub 2007 Apr 26. Gene Ther. 2007. PMID: 17460717

9

Mannitol-facilitated CNS entry of rAAV2 vector significantly delayed the neurological disease progression in MPS IIIB mice.

McCarty DM, DiRosario J, Gulaid K, Muenzer J, Fu H. McCarty DM, et al. Gene Ther. 2009 Nov;16(11):1340-52. doi: 10.1038/gt.2009.85. Epub 2009 Jul 9. Gene Ther. 2009. PMID: 19587708 Free PMC article.

10

Feasibility and safety of systemic rAAV9-hNAGLU delivery for treating mucopolysaccharidosis IIIB: toxicology, biodistribution, and immunological assessments in primates.

Murrey DA, Naughton BJ, Duncan FJ, Meadows AS, Ware TA, Campbell KJ, Bremer WG, Walker CM, Goodchild L, Bolon B, La Perle K, Flanigan KM, McBride KL, McCarty DM, Fu H. Murrey DA, et al. Among authors: mccarty dm. Hum Gene Ther Clin Dev. 2014 Jun;25(2):72-84. doi: 10.1089/humc.2013.208. Epub 2014 Apr 10. Hum Gene Ther Clin Dev. 2014. PMID: 24720466 Free PMC article.

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