Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation

Search Page

Filters

My Custom Filters

Publication date

Text availability

Article attribute

Article type

Additional filters

Article Language

Species

Sex

Age

Other

Search Results

112 results

Filters applied: . Clear all
Results are displayed in a computed author sort order. The Publication Date timeline is not available.
Page 1
Progress in gene therapy for neurological disorders.
Simonato M, Bennett J, Boulis NM, Castro MG, Fink DJ, Goins WF, Gray SJ, Lowenstein PR, Vandenberghe LH, Wilson TJ, Wolfe JH, Glorioso JC. Simonato M, et al. Among authors: vandenberghe lh. Nat Rev Neurol. 2013 May;9(5):277-91. doi: 10.1038/nrneurol.2013.56. Epub 2013 Apr 23. Nat Rev Neurol. 2013. PMID: 23609618 Free PMC article. Review.
Dosage thresholds for AAV2 and AAV8 photoreceptor gene therapy in monkey.
Vandenberghe LH, Bell P, Maguire AM, Cearley CN, Xiao R, Calcedo R, Wang L, Castle MJ, Maguire AC, Grant R, Wolfe JH, Wilson JM, Bennett J. Vandenberghe LH, et al. Sci Transl Med. 2011 Jun 22;3(88):88ra54. doi: 10.1126/scitranslmed.3002103. Sci Transl Med. 2011. PMID: 21697530 Free PMC article.
Gene therapy: charting a future course--summary of a National Institutes of Health Workshop, April 12, 2013.
O'Reilly M, Federoff HJ, Fong Y, Kohn DB, Patterson AP, Ahmed N, Asokan A, Boye SE, Crystal RG, De Oliveira S, Gargiulo L, Harper SQ, Ikeda Y, Jambou R, Montgomery M, Prograis L, Rosenthal E, Sterman DH, Vandenberghe LH, Zoloth L, Abedi M, Adair J, Adusumilli PS, Goins WF, Gray J, Monahan P, Popplewell L, Sena-Esteves M, Tannous B, Weber T, Wierda W, Gopal-Srivastava R, McDonald CL, Rosenblum D, Corrigan-Curay J. O'Reilly M, et al. Among authors: vandenberghe lh. Hum Gene Ther. 2014 Jun;25(6):488-97. doi: 10.1089/hum.2014.045. Hum Gene Ther. 2014. PMID: 24773122 Free PMC article. Review.
AAV9 targets cone photoreceptors in the nonhuman primate retina.
Vandenberghe LH, Bell P, Maguire AM, Xiao R, Hopkins TB, Grant R, Bennett J, Wilson JM. Vandenberghe LH, et al. PLoS One. 2013;8(1):e53463. doi: 10.1371/journal.pone.0053463. Epub 2013 Jan 30. PLoS One. 2013. PMID: 23382846 Free PMC article.
What Is Next for Retinal Gene Therapy?
Vandenberghe LH. Vandenberghe LH. Cold Spring Harb Perspect Med. 2015 Apr 15;5(10):a017442. doi: 10.1101/cshperspect.a017442. Cold Spring Harb Perspect Med. 2015. PMID: 25877395 Free PMC article. Review.
112 results