Safety and efficacy of mitapivat in sickle cell disease (RISE UP): results from the phase 2 portion of a global, double-blind, randomised, placebo-controlled trial.
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Lancet Haematol. 2024 Dec 4:S2352-3026(24)00319-3. doi: 10.1016/S2352-3026(24)00319-3. Online ahead of print.
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PMID: 39644907