The DcpS inhibitor RG3039 improves survival, function and motor unit pathologies in two SMA mouse models.
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Hum Mol Genet. 2013 Oct 15;22(20):4084-101. doi: 10.1093/hmg/ddt258. Epub 2013 Jun 4.
Hum Mol Genet. 2013.
PMID: 23736298
Free PMC article.