Therapeutic RNAi targeting PCSK9 acutely lowers plasma cholesterol in rodents and LDL cholesterol in nonhuman primates.
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Frank-Kamenetsky M, et al. Among authors: maier m.
Proc Natl Acad Sci U S A. 2008 Aug 19;105(33):11915-20. doi: 10.1073/pnas.0805434105. Epub 2008 Aug 11.
Proc Natl Acad Sci U S A. 2008.
PMID: 18695239
Free PMC article.