Safety and efficacy of deferiprone for pantothenate kinase-associated neurodegeneration: a randomised, double-blind, controlled trial and an open-label extension study.
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Klopstock T, et al. Among authors: zhao f.
Lancet Neurol. 2019 Jul;18(7):631-642. doi: 10.1016/S1474-4422(19)30142-5.
Lancet Neurol. 2019.
PMID: 31202468
Clinical Trial.