Base editing-mediated splicing correction therapy for spinal muscular atrophy.
Lin X, Chen H, Lu YQ, Hong S, Hu X, Gao Y, Lai LL, Li JJ, Wang Z, Ying W, Ma L, Wang N, Zuo E, Yang H, Chen WJ.
Lin X, et al. Among authors: li jj.
Cell Res. 2020 Jun;30(6):548-550. doi: 10.1038/s41422-020-0304-y. Epub 2020 Mar 24.
Cell Res. 2020.
PMID: 32210360
Free PMC article.
No abstract available.