Smith AJ - Search Results

1

Retraction Note: Gene therapy with a promoter targeting both rods and cones rescues retinal degeneration caused by AIPL1 mutations.

Sun X, Pawlyk B, Xu X, Liu X, Bulgakov OV, Adamian M, Sandberg MA, Khani SC, Tan M-, Smith AJ, Ali RR, Li T. Sun X, et al. Among authors: smith aj. Gene Ther. 2024 Nov 15. doi: 10.1038/s41434-024-00505-6. Online ahead of print. Gene Ther. 2024. PMID: 39548238 No abstract available.

2

Gene therapy with a promoter targeting both rods and cones rescues retinal degeneration caused by AIPL1 mutations.

Sun X, Pawlyk B, Xu X, Liu X, Bulgakov OV, Adamian M, Sandberg MA, Khani SC, Tan MH, Smith AJ, Ali RR, Li T. Sun X, et al. Among authors: smith aj. Gene Ther. 2010 Jan;17(1):117-31. doi: 10.1038/gt.2009.104. Epub 2009 Aug 27. Gene Ther. 2010. Retraction in: Gene Ther. 2024 Nov 15. doi: 10.1038/s41434-024-00505-6 PMID: 19710705 Free PMC article. Retracted.

3

Photoreceptor rescue by an abbreviated human RPGR gene in a murine model of X-linked retinitis pigmentosa.

Pawlyk BS, Bulgakov OV, Sun X, Adamian M, Shu X, Smith AJ, Berson EL, Ali RR, Khani S, Wright AF, Sandberg MA, Li T. Pawlyk BS, et al. Among authors: smith aj. Gene Ther. 2016 Feb;23(2):196-204. doi: 10.1038/gt.2015.93. Epub 2015 Sep 8. Gene Ther. 2016. PMID: 26348595 Free PMC article.

4

Intraocular gene delivery of ciliary neurotrophic factor results in significant loss of retinal function in normal mice and in the Prph2Rd2/Rd2 model of retinal degeneration.

Schlichtenbrede FC, MacNeil A, Bainbridge JW, Tschernutter M, Thrasher AJ, Smith AJ, Ali RR. Schlichtenbrede FC, et al. Among authors: smith aj. Gene Ther. 2003 Mar;10(6):523-7. doi: 10.1038/sj.gt.3301929. Gene Ther. 2003. PMID: 12621456

5

Long-term preservation of retinal function in the RCS rat model of retinitis pigmentosa following lentivirus-mediated gene therapy.

Tschernutter M, Schlichtenbrede FC, Howe S, Balaggan KS, Munro PM, Bainbridge JW, Thrasher AJ, Smith AJ, Ali RR. Tschernutter M, et al. Among authors: smith aj. Gene Ther. 2005 Apr;12(8):694-701. doi: 10.1038/sj.gt.3302460. Gene Ther. 2005. PMID: 15660111

6

Gene replacement therapy rescues photoreceptor degeneration in a murine model of Leber congenital amaurosis lacking RPGRIP.

Pawlyk BS, Smith AJ, Buch PK, Adamian M, Hong DH, Sandberg MA, Ali RR, Li T. Pawlyk BS, et al. Among authors: smith aj. Invest Ophthalmol Vis Sci. 2005 Sep;46(9):3039-45. doi: 10.1167/iovs.05-0371. Invest Ophthalmol Vis Sci. 2005. PMID: 16123399

7

Gene supplementation therapy for recessive forms of inherited retinal dystrophies.

Smith AJ, Bainbridge JW, Ali RR. Smith AJ, et al. Gene Ther. 2012 Feb;19(2):154-61. doi: 10.1038/gt.2011.161. Epub 2011 Oct 27. Gene Ther. 2012. PMID: 22033465 Review.

8

The Future Looks Brighter After 25 Years of Retinal Gene Therapy.

Auricchio A, Smith AJ, Ali RR. Auricchio A, et al. Among authors: smith aj. Hum Gene Ther. 2017 Nov;28(11):982-987. doi: 10.1089/hum.2017.164. Epub 2017 Aug 20. Hum Gene Ther. 2017. PMID: 28825330 Review.

9

Stable rAAV-mediated transduction of rod and cone photoreceptors in the canine retina.

Bainbridge JW, Mistry A, Schlichtenbrede FC, Smith A, Broderick C, De Alwis M, Georgiadis A, Taylor PM, Squires M, Sethi C, Charteris D, Thrasher AJ, Sargan D, Ali RR. Bainbridge JW, et al. Among authors: smith a. Gene Ther. 2003 Aug;10(16):1336-44. doi: 10.1038/sj.gt.3301990. Gene Ther. 2003. PMID: 12883530

10

Assessment of ocular transduction using single-stranded and self-complementary recombinant adeno-associated virus serotype 2/8.

Natkunarajah M, Trittibach P, McIntosh J, Duran Y, Barker SE, Smith AJ, Nathwani AC, Ali RR. Natkunarajah M, et al. Among authors: smith aj. Gene Ther. 2008 Mar;15(6):463-7. doi: 10.1038/sj.gt.3303074. Epub 2007 Nov 15. Gene Ther. 2008. PMID: 18004402

Save citations to file

Email citations

Send citations to clipboard

Add to Collections

Add to My Bibliography

Create a file for external citation management software

Your saved search

Your RSS Feed

My Custom Filters

Publication date

Text availability

Article attribute

Article type

Article Language

Species

Sex

Age

Other

2,169 results

Search Page

Filters