Rational design of ligands targeting triplet repeating transcripts that cause RNA dominant disease: application to myotonic muscular dystrophy type 1 and spinocerebellar ataxia type 3.
J Am Chem Soc. 2009 Jul 22;131(28):9767-79. doi: 10.1021/ja9020149.
J Am Chem Soc. 2009.
PMID: 19552411
Free PMC article.