R01 HL070135/HL/NHLBI NIH HHS/United States[Grants and Funding] - Search Results

Save citations to file

Email citations

Your saved search

Your RSS Feed

Page 1

A novel human gamma-globin gene vector for genetic correction of sickle cell anemia in a humanized sickle mouse model: critical determinants for successful correction.

Perumbeti A, Higashimoto T, Urbinati F, Franco R, Meiselman HJ, Witte D, Malik P. Perumbeti A, et al. Blood. 2009 Aug 6;114(6):1174-85. doi: 10.1182/blood-2009-01-201863. Epub 2009 May 27. Blood. 2009. PMID: 19474450 Free PMC article.

Reprogramming erythroid cells for lysosomal enzyme production leads to visceral and CNS cross-correction in mice with Hurler syndrome.

Wang D, Zhang W, Kalfa TA, Grabowski G, Davies S, Malik P, Pan D. Wang D, et al. Proc Natl Acad Sci U S A. 2009 Nov 24;106(47):19958-63. doi: 10.1073/pnas.0908528106. Epub 2009 Nov 10. Proc Natl Acad Sci U S A. 2009. PMID: 19903883 Free PMC article.

Mechanism of reduction in titers from lentivirus vectors carrying large inserts in the 3'LTR.

Urbinati F, Arumugam P, Higashimoto T, Perumbeti A, Mitts K, Xia P, Malik P. Urbinati F, et al. Mol Ther. 2009 Sep;17(9):1527-36. doi: 10.1038/mt.2009.89. Epub 2009 Apr 21. Mol Ther. 2009. PMID: 19384292 Free PMC article.

Genotoxic potential of lineage-specific lentivirus vectors carrying the beta-globin locus control region.

Arumugam PI, Higashimoto T, Urbinati F, Modlich U, Nestheide S, Xia P, Fox C, Corsinotti A, Baum C, Malik P. Arumugam PI, et al. Mol Ther. 2009 Nov;17(11):1929-37. doi: 10.1038/mt.2009.183. Epub 2009 Aug 25. Mol Ther. 2009. PMID: 19707188 Free PMC article.

The 3' region of the chicken hypersensitive site-4 insulator has properties similar to its core and is required for full insulator activity.

Arumugam PI, Urbinati F, Velu CS, Higashimoto T, Grimes HL, Malik P. Arumugam PI, et al. PLoS One. 2009 Sep 10;4(9):e6995. doi: 10.1371/journal.pone.0006995. PLoS One. 2009. PMID: 19746166 Free PMC article.

Save citations to file

Email citations

Send citations to clipboard

Add to Collections

Add to My Bibliography

Create a file for external citation management software

Your saved search

Your RSS Feed

My Custom Filters

Publication date

Text availability

Article attribute

Article type

Article Language

Species

Sex

Age

Other

5 results

Search Page

Filters